Project Details
Description
This research project will pave the way for future NF human gene therapy while building fundamental gene editing and vector delivery technologies. While our goal is to transform the treatment of individuals with NF1 and NF2, new CRISPR enzymes and AAV vectors will be broadly applicable for a range of other genetic conditions
| Status | Active |
|---|---|
| Effective start/end date | 1/01/24 → 31/12/27 |
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